WDO Webinar: Gene Therapy in Duchenne Muscular Dystrophy

The WDO webinar on 'Gene Therapy in Duchenne Muscular Dystrophy,' held on November 7, 2023, delved into crucial aspects of gene therapy for DMD patients.

Topics:
3:11 How gene therapy works – Prof Annemieke Aartsma-Rus
30:43 Managing serious adverse events (SAE) – Prof Eugenio Mercuri
50:38 Immune responses in gene therapy – Prof Francesco Muntoni
1:10:59 Gene therapy and the heart – Dr Chet Villa, MD
1:46:16 Gene therapy landscape and clinical trials – Company presentations
2:30:38 Access and reimbursement: The SMA experience – Mencía de Lemus Belmonte

© 2023 World Duchenne Organization.

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