Avidity Biosciences - Meet the DM Drug Developers 2024

Presented on March 15, 2024.

Join us for a Meet the Myotonic Dystrophy Drug Developers webinar with Avidity Biosciences! Don't miss this special presentation on the "Global Phase 3 HARBOR Study & Long-term MARINA-OLE Data".

Learn more about Avidity Biosciences at https://www.aviditybiosciences.com/

Panelists include:
+ Sarah Boyce, President & CEO, & Member of the Board of Directors, Avidity Biosciences
+ Li-Jung Tai, MD, PhD, Executive Director in Clinical Development, Avidity Biosciences
+ Kath Gallagher, Senior Vice President and Global Program Head, Myotonic Dystrophy Type 1, Avidity Biosciences
+ John Day MD, PhD, Professor of Neurology, Pediatrics (Genetics) and Pathology, and Director of the Division of Neuromuscular Medicine, Stanford School of Medicine

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About MDF's Meet the DM Drug Developers Webinar Series

Our biotechnology, pharmaceutical and academic partners, large and small, working on treatments and a cure for myotonic dystrophy will sit down with our community to share their progress and answer your questions.

Find all our upcoming Meet the DM Drug Developers dates and previously recorded sessions at www.myotonic.org/meet-dm-drug-developers

Learn more about myotonic dystrophy at https://www.myotonic.org/

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MDF Resources referenced in this video:

Toolkits & Publications - https://www.myotonic.org/toolkits-pub...

Support Groups - https://www.myotonic.org/find-support

Digital Academy - https://www.myotonic.org/digital-academy

Calendar of Events - https://www.myotonic.org/calendar/month

2024 MDF Regional Conferences - https://www.myotonic.org/2024-mdf-reg...

Sign up for My Dispatch, our monthly e-newsletter - https://www.myotonic.org/sign-emails-0

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0:00:00 Welcome & MDF Resource Highlights
0:03:18 An Overview of Myotonic Dystrophy Drug Development
0:07:20 Speaker Introduction
0:10:01 Avidity Biosciences Overview & Agenda
0:17:52 Upcoming HARBOR(TM) Global Phase 3 Study
0:22:53 In-Progress MARINA-OLE(TM) Study Results
0:41:34 Transforming the Future of DM1 Together
0:52:26 Question & Answer Session
1:15:09 Thank You for Attending