Скачать или смотреть CNS Symptoms and Meaningful Clinical Trial Endpoints - 2025 MDF Conference

A summary from the clinical endpoint workshop focusing on CNS clinical presentations and meaningful endpoints in clinical trials for myotonic dystrophy

Presenter:
Eric Wang, PhD, Associate Professor, Molecular Genetics & Microbiology, University of Florida, MDF Medical and Scientific Advisory Committee, MDF National Advocacy Committee

Explore our other sessions and read about the incredible 2025 MDF Conference in Indianapolis, Indiana: https://www.myotonic.org/over-700-peo...

Learn more about myotonic dystrophy and the Myotonic Dystrophy Foundation (MDF) at https://www.myotonic.org/

Chapters:
0:00:00 - Introduction
0:05:54 - Study Focus
0:16:34 - Why we need CNS endpoints & clinical trials
0:17:27 - How do we work together to reach goals?
0:22:57 - Summary
0:23:27 - Q&A