Gene Therapy 101: What Is It and How Can It Help Us Treat Rare Genetic Disorders?

What if a therapy could treat more than just the symptoms of a rare genetic disorder? What if it could address its underlying genetic cause and repair a body’s defective gene? What if this therapy could work with a single treatment rather than a lifetime’s worth of medication?

At PTC, we study human genes with a mission to treat rare genetic disorders. Connect with us!

Visit Our Website: https://www.ptcbio.com
Subscribe to the PTC Channel on YouTube: https://bit.ly/PTCYouTube
Learn More About Clinical Trials: https://clinicaltrials.ptcbio.com/en/
Investor Relations: https://ir.ptcbio.com/
Follow PTC on LinkedIn:   / ptc-therapeutics  
Like PTC on Facebook:   / ptctherapeutics  
Like PTC on Instagram:   / ptctherapeutics  
Follow PTC on Twitter:   / ptcbio  
Apply for a Career with Purpose at PTC: https://www.ptcbio.com/careers/career...
Email for patients and families: [email protected]
Email for Health Care Providers: [email protected]
All Other Inquiries: [email protected]

About PTC Therapeutics, Inc. PTC is a science-driven, global biopharmaceutical company focused on the discovery, development and commercialization of clinically differentiated medicines that provide benefits to patients with rare disorders. PTC's ability to globally commercialize products is the foundation that drives investment in a robust and diversified pipeline of transformative medicines and our mission to provide access to best-in-class treatments for patients who have an unmet medical need.